Title: Advances in Gene Therapy – 2024 Update
Sponsored by The Therapeutics Committee
Date of Release: July 2, 20024
Expiration Date: July 2, 20026
Credits offered: CME
Estimate time of completion: 1 hour per webinar
Course must be completed by the expiration date
www.acmgeducation.net
Description:
Access our on-demand webinar, a follow-up to the 2022 Summer Gene Therapy Webinar, featuring essential updates and in-depth insights on groundbreaking advancements in gene therapy. Stay up to date on cutting-edge innovations shaping the future of genetic medicine.
Target Audience: This webinar is designed for trainees, medical geneticists, biochemical geneticists,
neurologists, and laboratory geneticists who are eager to stay at the forefront of gene therapy advancements.
Presentation
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Presenter
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Welcome and Introduction
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Kuntal Sen, MD, FACMG| Jaya Ganesh, MD, FACMG
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Gene Therapy and Genome Editing - An Overview
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Dwight Koeberl, MD, PhD, FACMG
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Gene Therapy Updates in Neuromuscular and Neurometabolic Disorders
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Stephen M. Chrzanowski, MD, PhD
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Gene Therapy: Towards Transformative Care for Sickle Cell Disease
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Harry Layton Lesmana, MD, FACMG
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Learning Objectives
At the conclusion of this session, participants should be able to:
- Expand Knowledge on CRISPR and Gene Replacement Therapy: Provide comprehensive updates on the latest developments in CRISPR technology and gene replacement therapy, focusing on how these innovations are shaping the future of genetic medicine.
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- Review New Pediatric Neurogenetic Therapies: Examine recently approved gene therapies for pediatric neurogenetic conditions such as Metachromatic Leukodystrophy (MLD), Duchenne Muscular Dystrophy (DMD), and X-linked Adrenoleukodystrophy (XALD). Discuss their clinical applications, efficacy, and impact on patient outcomes.
- Discuss Gene Therapy for Sickle Cell Disease: Delve into the specifics of gene therapy for sickle cell disease, exploring the underlying mechanisms and therapeutic potential. Highlight case studies and clinical trial results to illustrate the transformative effects of these treatments.
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- Analyze Financial and Ethical Considerations: Address the economic aspects and ethical implications of gene therapy. Evaluate the cost-effectiveness, accessibility, and ethical challenges associated with these advanced therapies to foster informed decision-making among healthcare professionals and patients.