Stephanie Austin, MS, CGC
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Employee: Amicus Therapeutics, Ins.
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John A. Bernat, MD, PhD, FACMG
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Research support for clinical trials: Avrobio, BioMarin Pharmaceutical Inc., Idorsia Pharmaceuticals, Pfizer, Inc., Protalix Biotherapeutics, Sangamo Therapeutics, Sanofi, Takeda Pharmaceutical, Travere Therapeutics, Inc.
SAB: Sanofi, Takeda Pharmaceutical
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Lindsay C. Burrage, MD, PhD, FACMG
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Nothing to disclose
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Irene J. Chang, MD, FACMG
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Nothing to disclose
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Stephen M. Chrzanowski, MD, PhD
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Nothing to Disclose
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Haiyan Fu, PhD
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Nothing to disclose
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Jaya Ganesh, MD, FACMG
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Research: BioMarin Pharmaceutical, Denali Therapeutics, Sangamo, Sanofi Genzyme, Takeda Pharmaceutical, Travere Therapeutics, Inc.
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Brett H. Graham, MD, PhD, FACMG
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Nothing to disclose
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Dwight Koeberl, MD, PhD, FACMG
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Stock: Asklepios BioPharmaceutical (AskBio)
Consultant: Moderna
DSMB: Baxalta
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Harry Layton Lesmana, MD, FACMG
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Consultant: Pharming Healthcare, Inc.
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Gerald S. Lipshutz, MD, PhD
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DSMB: Astellas Pharma
Consultant: Taysha
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Loren D. Pena, MD, PhD, FACMG
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Consultant: Novartis Gene Therapies, Inc., Orphazyme, Sanofi US Services, Inc., Ultragenyx Pharmaceutical Inc.
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Jane Radford, MHA, CHCP
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Nothing to disclose
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Kuntal Sen, MBBS, FACMG
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Nothing to disclose
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Amy Siemon, MS
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Nothing to disclose
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Hadley Smith, PhD, MPSA
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Consultant: Illumina, Inc.
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Charles P. Venditti MD, PhD
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Grant/Contract: Selecta Biosciences
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Jerry Vockley, MD, PhD, FACMG
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Grants/Contracts: LogicBio Therapeutics, Homology Pharmaceuticals, Reneo Pharmaceuticals, Hemoshear Pharmaceuticals, BioMarin Pharmaceutical Inc., CoA Therapeutics, Nestle HealthCare Nutrition Inc., Synlogic Pharmaceuticals, 4D Molecular Therapeutics, Moderna Pharmaceuticals, Ultragenyx Pharmaceutical Inc., Aeglea BioTherapeutics, Stealth Pharmaceuticals
Consultant: BioMarin Pharmaceutical Inc., Applied Therapeutics, LogicBio Therapeutics, Agios Pharmaceuticals, Inc., Axcella Health, Orphan Labs, Sangamo Therapeutics, Synlogic Pharmaceuticals, Sanofi Pasteur Biologics, LLC, Ecrol Capital, Frictionless Solutions
Stock: American Gene Technologies
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