**ACMG Education Webinar Series: Translating Genes into Health®**

Discover the latest in genetic healthcare through expert-led webinars aligned with ACMG’s strategic priorities and learner needs.

OnDemand access will be available following each live event. Complimentary for ACMG members, with a nominal fee for non-members.

Registration is free.

Jan

2026 Gene Therapy Bootcamp - Application in Neurodevelopment Disorders

Hosted by The Education and Professional Development Committee

Explore the evolving landscape of gene therapy, including gene replacement, gene editing, and other nucleic-acid–based approaches. This session will provide a practical, clinically oriented update on the latest developments and their implications for medical genetics practice in 2026. Speakers will highlight applications in neurodevelopmental disorders and showcase the FDA-approved gene therapy ladocagene exuparvovec-tneq, while addressing key considerations such as underlying genetic mechanisms, dosage windows, preclinical modeling, clinical endpoints, biomarkers, and risk-benefit assessment.

Feb

The Horizon of Prenatal Therapies for genetic Disorders

Hosted by The Education and Professional Development Committee

Learn about the evolving therapies available to treat fetuses affected by complicated genetic disorders. In this session, presenters will review the fetal presentation of lysosomal storage disorders (LSDs) and spinal muscular atrophy (SMA) and discuss novel therapeutic strategies including an ongoing phase 1 clinical trial of in utero enzyme replacement for LSDs and the prenatal use of an SMN2 splicing modifier to treat fetuses with SMA.

Presenters:

Billie Lianoglou, CGC

University of California, San Francisco

Richard Finkel, MD

St. Jude Children’s Research Hospital