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July 16 - Advances in Gene Therapy – 2024 Update
July 16 - Advances in Gene Therapy – 2024 Update
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The "Advances in Gene Therapy – 2024 Update" session highlighted several key themes and trends, reflecting the differing roles and perspectives of its participants. A notable proportion, 44.8%, reported not having direct patient-facing roles, representing students, researchers, and professionals in non-clinical settings. Education emerged as a vital focus, with 24.1% of respondents emphasizing keeping informed of new treatments and incorporating this knowledge into patient education and curricula.<br /><br />A cautious approach was advised by 6.9% of respondents, who noted the novelty of gene therapies and the need for more comprehensive data before widespread adoption. Conversely, 21.8% of participants were eager to apply newfound insights to patient care, particularly in educating patients about cutting-edge therapies for conditions like Duchenne Muscular Dystrophy (DMD) and Sickle Cell Disease.<br /><br />Survey feedback indicated high approval rates, with 95.37% of participants feeling the presentation met their expectations. Positive comments praised the session's comprehensive content and practical insights, with 57.7% expressing satisfaction and 23.1% appreciating updates from previous series. There were calls for improvement, such as suggestions to provide slides for download and record sessions for those unable to attend live.<br /><br />Finally, the session underscored the educational objectives, emphasizing the potential of CRISPR and gene replacement therapy in shaping future genetic medicine. Attendees highlighted the economic and ethical dimensions of gene therapy, advocating for informed decision-making. The feedback included calls for more practical clinical examples to bridge the gap between theory and application in real-world settings.
Keywords
Gene Therapy
Education
CRISPR
Patient Care
Duchenne Muscular Dystrophy
Sickle Cell Disease
Clinical Application
Ethical Considerations
Genetic Medicine
Survey Feedback
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